Blog
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About Gaucher Disease
Gene Therapy for Gaucher Disease: AAV, Lentivirus, & More
Gaucher disease occurs when people have mutations, or changes, in... Read more
Blog
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About Gaucher Disease
Gaucher Disease and Myeloma: What Patients and Families Should Know
Two thirds of Gaucher patients have some evidence of bone... Read more
Blog
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About Gaucher Disease
Gaucher Disease: How Peer Support and Empowerment Can Help
Rare diseases can affect all aspects of a patient’s life,... Read more
Blog
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About Gaucher Disease
What Is Our Impact? – NGF 2019 Impact Report
In our 2019 Impact Report, we take a look at... Read more
News
AVROBIO Receives Orphan-Drug Designation from FDA for AVR‑RD‑02
AVROBIO announced that the U.S. Food and Drug Administration (FDA)... Read more
Blog
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About Gaucher Disease
Developing Enzyme Replacement Therapy – An Insider’s Perspective
Enzyme replacement therapy (ERT) was first approved for use by... Read more
Blog
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About Gaucher Disease
[MEDTalks Video] Managing Bone Health
Growth in Gaucher: Managing Bone Health Dr. Heather A. Lau,... Read more
Blog
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About Gaucher Disease
[MEDTalks Video] Does the Key Biomarker of Gaucher Disease Hold the Key to Understanding?
Illuminating Lyso-Gyl 1: Does the Key Biomarker of Gaucher Disease... Read more
Blog
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About Gaucher Disease
Clinical Trials & Gaucher Disease: Phases, Types, & What You Should Know
Medical research has always been important for furthering our understanding... Read more
Blog
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Insurance
Repealing the Affordable Care Act
How Repealing the ACA Could Impact the Gaucher Disease... Read more
