NGF Blog

Blog / Patient Journeys

Gaucher Journey: Rivka Silver

Want to share your story? Contact us and we’ll be... Read more

Blog / Patient Journeys

Gaucher Journey: Morán Family

Want to share your story? Contact us and we’ll be... Read more

Ambroxol, a glucocerebrosidase (GCase) activator, represents a potential new treatment for the most severe neurological symptoms of Gaucher disease.
Blog / About Gaucher Disease

Ambroxol: New Use as a Gaucher Disease Treatment?

Research on the medication Ambroxol and other existing drugs with... Read more

Cannabis for Gaucher disease pain
Blog / About Gaucher Disease

Cannabis for Gaucher Disease Pain

Chronic joint pain is a common symptom of Gaucher disease.... Read more

Hands holding a drawing of a fetus
Blog / About Gaucher Disease

Ashkenazi Jewish Prenatal Genetic Screening: What Future Parents Should Know

People of Ashkenazi Jewish descent have a higher risk of... Read more

Research on small molecule therapy a potential treatment for Gaucher disease
Blog / About Gaucher Disease

Small Molecule Therapy for Gaucher Disease and GBA1-Associated Parkinson’s Disease

Mutations of the GBA gene cause Gaucher disease and are... Read more

Patient receiving therapy for Gaucher disease.
Blog / About Gaucher Disease

Enzyme Replacement Therapy for Gaucher Disease: Frequently Asked Questions

People with Gaucher disease, an inherited condition, don’t make enough... Read more

A fetal therapy for Gaucher disease clinical trial offers new hope for expecting couples
Blog / About Gaucher Disease

Fetal Therapy for Gaucher Disease

Gaucher disease causes glucocerebroside to build up in cells, which... Read more

Blog / About the National Gaucher Foundation

NGF Global Diagnostic and Treatment Initiative Heads to India

Dr. Robin A. Ely, Clinical/Science Advisor, Director of the National... Read more

Blog / Patient Journeys

Gaucher Journey: Shauna Mangum

Want to share your story? Contact us and we’ll be... Read more

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