NGF Blog


Gain Therapeutics, Inc. Announces Positive Topline Data in Patient-derived iPSC Study Evaluating STAR Compounds as a Treatment for Gaucher and Parkinson’s Disease

GT-02287and GT-02329 compounds display positive effects on GCase activity and... Read more

Blog / About Gaucher Disease

9 Myths About Genetic Disease Carrier Screening

Health and family planning are deeply personal. Above all, everyone... Read more


AVROBIO Reports Second Quarter 2021 Financial Results and Provides Business Update

U.S. Food and Drug Administration granted Fast Track Designation to... Read more

Blog / Living With Gaucher Disease

Gaucher Disease and Reproductive Health

Living with a chronic hereditary condition like Gaucher disease can... Read more

Blog / Insurance

How the American Rescue Plan and State Health Insurance Laws Affect You

As the U.S. moves toward reopening in the wake of... Read more


Gain Therapeutics Announces Issuance of Two New PCT Patents Covering GBA and GALC Modulator Compounds for Treatment of CNS Disorders

Activity of GBA and GALC Enzymes Play Key Roles in... Read more

Blog / Living With Gaucher Disease

Supporting Transition from Pediatrics to Adult Healthcare

For any family, it can be intimidating to launch a... Read more

Blog / About Gaucher Disease

GBA gene: Parkinson’s Disease and the Gaucher Community

Gaucher disease results when an individual inherits two mutations in... Read more

Blog / About Gaucher Disease

How Does Nutrition Affect the Immune System

Nutrition and your immune system are intimately connected. That fact... Read more


Takeda Announces Creation of the Rare Disease Clinical Activity Protocols (Rare-CAP) program

A Five-year Commitment From Takeda Will Help Children’s National Launch... Read more

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