Committing to Care, Access, Equity, and Research: NORD Announces 31 Rare Disease Centers of Excellence
NORD provides new designation to medical centers to define standards... Read more
How Systemic Inflammation Affects Your Brain & Central Nervous System
Bodies are like well-oiled machines, with many systems that work... Read more
Newborn Screening: What You Need to Know
People living with an inheritable disorder like Gaucher disease understand... Read more
Gain Therapeutics, Inc. Announces Positive Topline Data in Patient-derived iPSC Study Evaluating STAR Compounds as a Treatment for Gaucher and Parkinson’s Disease
GT-02287and GT-02329 compounds display positive effects on GCase activity and... Read more
9 Myths About Genetic Disease Carrier Screening
Health and family planning are deeply personal. Above all, everyone... Read more
AVROBIO Reports Second Quarter 2021 Financial Results and Provides Business Update
U.S. Food and Drug Administration granted Fast Track Designation to... Read more
Gaucher Disease and Reproductive Health
Living with a chronic hereditary condition like Gaucher disease can... Read more
How the American Rescue Plan and State Health Insurance Laws Affect You
As the U.S. moves toward reopening in the wake of... Read more
Gain Therapeutics Announces Issuance of Two New PCT Patents Covering GBA and GALC Modulator Compounds for Treatment of CNS Disorders
Activity of GBA and GALC Enzymes Play Key Roles in... Read more
Supporting Transition from Pediatrics to Adult Healthcare
For any family, it can be intimidating to launch a... Read more
