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Gaucher Disease News at a Glance

May 27, 2015 - Stem Cell Treatment Speeds Up Recovery after Spinal Cord Injury in Monkeys

May 25, 2015 - Group releases strategy to help Canadians with rare diseases get care.

May 24, 2015 - Hatch, Klobuchar propose law to foster development of rare disease treatments

May 20, 2015 - Genzyme’s Announces Launch of Expression of Hope III Art Exhibit

May 19, 2015 - Genzyme Receives Innovation Award from the National Organization for Rare Disorders (NORD) for the Development of Cerdelga®

May 18, 2015 - Hospital to create emergency experiences using virtual reality: walk around inside crisis situations, educate medical professionals

May 14, 2015 - Environmental Nutrition: A is for Asparagus

May 14, 2015 - Eggs: Health Benefits & Nutrition Facts

May 13, 2015 - Nutrition Q&A: Healthy lunch options for work

May 13, 2015 - Women's Health and Undernutrition in the U.S.

May 12, 2015 - High prices for drugs to treat rare diseases take a toll

May 7, 2015 - Shire ACES Scholarship Program

May 4, 2015 - Penury and rare disease make the lives of 72 million grim

Apr 27, 2015 - Food labels moved to front of packages shown to improve consumer’s food choices.

Apr 27, 2015 - Better living starts with you

Apr 27, 2015 - The Top 10 Supermarket Foods to Avoid for Good Nutrition

Apr 26, 2015 - Variants associated with Gaucher disease in multiple system atrophy

Apr 24, 2015 - Sangamo BioSciences Presents Data At 11th Annual WorldSymposium™ Meeting Supporting In Vivo Protein Replacement Platform Approach For The Treatment Of Lysosomal Storage Disorders

Apr 23, 2015 - Genetic Alliance presents virtual session for advocates

Apr 23, 2015 - Emory University LSDC Program Program Survey

Apr 23, 2015 - Running On Rose Petals

Apr 21, 2015 - Specialty Drugs Dominate Late-Stage Pipeline

Apr 20, 2015 - Genetic Alliance to Coordinate PCORI’s Patient Powered Research Networks

Apr 14, 2015 - 8 Things You Should Know About GMOs

Apr 13, 2015 - Improving nutrition in cancer survivors

Apr 12, 2015 - The GP diet: the missing ingredient in better health

Apr 12, 2015 - Most food misses mark

Apr 12, 2015 - Chow Line: Why choose whole foods over processed?

Apr 12, 2015 - Nutrition necessary for performance, health

Apr 2, 2015 - 13-year-old, Bennett Resnick of West Chester, PA raises $1,500 for the NGF's Awareness Campaign, "No Way Gaucher”

Mar 31, 2015 - N.J. cheerleader soars to great heights, defying genetic disorder

Mar 31, 2015 - Beyond the Diagnosis Art Exhibit

Mar 30, 2015 - Genzyme’s Cerdelga® (eliglustat) Capsules Approved in Japan

Mar 28, 2015 - 24-year-old Atlanta Runner Beats Lymphoma

Mar 28, 2015 - Parkinson’s Life - a new 'webzine' for the international Parkinson's community, launching April 2015

Mar 26, 2015 - Genzyme Convenes Sixth Annual Gaucher Leadership Forum

Mar 26, 2015 - Drugs for rare diseases - Science, patients behind surge in more research

Mar 25, 2015 - Global Gaucher's Disease Epidemiology and Patient Flow Analysis - 2015

Mar 25, 2015 - Gaucher Presentation: Ozlem Goker-Alpan, MD - Overview and goals for current therapy

Mar 25, 2015 - ENCORE Clinical Data Published in The Lancet Suggest Treatment with Oral Maintenance Therapy Effective in Previously Treated Gaucher Disease Patients

Mar 24, 2015 - Parkinson's Biomarker Initiative Expands Genetic Study

Mar 24, 2015 - PPMI Now Recruiting Individuals with Genetic Mutation linked to Gaucher Disease

Mar 23, 2015 - Genzyme Horizons Spring 2015 Newsletter

Mar 22, 2015 - Global gaucher disease market to grow at a CAGR of 7.60% during 2014-2019

Mar 20, 2015 - Need to understand rare diseases: Kalam

Mar 19, 2015 - European Regulatory Roundup: Sanofi's Zerhouni Calls for Regulatory Harmonization

Mar 18, 2015 - People with Rare Diseases Hope Banding Together Will Help Their Cause

Mar 18, 2015 - The global gaucher disease market will exhibit moderate growth from 2014 to 2019

Mar 11, 2015 - Rare Disease United Foundation (RDUF) promotes awareness of rare diseases throughout the world

Mar 10, 2015 - Mount Pleasant doctor with cancer is advocate for other rare disease patients

Mar 10, 2015 - Genzyme Webcast about Cerdelga

Mar 6, 2015 - The Must-Have Collaborations for Successful Drug Development

Mar 4, 2015 - The Health Care Supreme Court Case: Who Would Be Affected?

Mar 3, 2015 - Any Exercise Is Good, But Higher-Intensity May Be Better

Mar 3, 2015 - First Grant Recipients from Million Dollar Bike Ride

Mar 3, 2015 - Seeking aid for their children

Mar 3, 2015 - Michigan highlights Rare Disease Day, recognizes importance of newborn screening

Mar 2, 2015 - California Healthcare Institute Spotlights Impact of Rare Diseases with Assembly member Katcho Achadjian

Mar 2, 2015 - Social Media Is A Lifeline For Patients With Rare Diseases

Feb 28, 2015 - World Rare Disease Day: How police's efforts saved a child from Gaucher's disease

Feb 27, 2015 - Patient Involvement Helps Pfizer Develop Orphan Drugs

Feb 27, 2015 - HC asks AIIMS to provide free treatment to genetic disorder patient

Feb 25, 2015 - Fair Pricing for 'Orphan' Medications

Feb 25, 2015 - New Report: Transforming Rare Disease Patients' Lives Through Innovation

Feb 19, 2015 - Idis and CheckOrphan Announce New Online Rare Disease Access Programs Register

Feb 18, 2015 - Rare Disease Explained in 7 Tweets

Feb 18, 2015 - Eliglustat decreases spleen size in Type I Gaucher disease [ENGAGE Trial]

Feb 18, 2015 - Help Jonathan Win the Great Bike Giveaway Being Held by Friendship Circle

Feb 17, 2015 - Hidden heart disease a stroke risk for younger women

Feb 17, 2015 - Cerdelga improves liver volume, other factors in Gaucher's disease

Feb 14, 2015 - Safety and Efficacy of ELELYSO® (taliglucerase alfa) for Injection in Pediatric Patients with Type 1 Gaucher Disease in Long-term Outcome Study Presented at the WORLDSymposium 2015

Feb 13, 2015 - Pfizer reports positive Phase III trial results of Type 1 Gaucher disease drug Elelyso

Feb 12, 2015 - Cerdelga Effective in Gaucher Disease Type 1 Study

Feb 12, 2015 - Genzyme Presents Phase 3 Clinical Trial Extension Results for Cerdelga® (eliglustat) at Lysosomal Disease Network’s WORLD Symposium 2015

Feb 12, 2015 - Pfizer (PFE) Updates on ELELYSO Phase 3 in Type 1 Gaucher at WORLDSymposium

Feb 11, 2015 - Pricing uncertainty for orphan drugs and innovative new drugs

Feb 9, 2015 - What’s Lurking in Your Herbal Supplement?

Feb 8, 2015 - Wdowik nutrition column: Vitamin D important for more than just bones

Feb 6, 2015 - Lentiviral gene therapy using cellular promoters cures type 1 Gaucher disease in mice

Feb 5, 2015 - Shuttling drugs across the blood-brain barrier

Feb 5, 2015 - Screening Newborns' DNA -- Why Not?

Feb 5, 2015 - Gaucher Disease is discussed on the television show, Healthy Mind and Body

Feb 3, 2015 - Lysosomal Therapeutics Inc. Raises $20 Million in Series A Financing

Feb 2, 2015 - Shire Joins the rare disease community in recognizing Rare Disease Day!

Feb 2, 2015 - Diet, Nutrition Closely Linked to Mental Health

Feb 1, 2015 - The Top Diet Trends for 2015

Feb 1, 2015 - Common Household Pesticides May Double Risk Of ADHD In Kids Exposed To Chemicals During Pregnancy, Breastfeeding

Jan 22, 2015 - Genzyme's oral Gaucher drug cleared in Europe Cerdelga now available to adults with type 1 Gaucher disease

Jan 21, 2015 - There's No Place Like Home

Jan 20, 2015 - What's What in Nutrition? What's on First

Jan 19, 2015 - Pizza cuts into kids' health, study finds

Jan 19, 2015 - School cafeterias use technology to create healthy eating 'report card'

Jan 18, 2015 - Exercise safety and performance

Jan 17, 2015 - Nutrition tip of the week: Examining 2015 food trends

Jan 14, 2015 - The National Organization for Rare Disorders Registries for Rare Diseases: Involve the Patient

Jan 14, 2015 - Breakthrough drug for rare genetic disease

Jan 13, 2015 - Orphan Drugs in the EU: A Record-Breaking Year

Jan 13, 2015 - Why the 100,000 Genomes Project will focus on rare diseases

Jan 12, 2015 - Mutant glucocerebrosidase in Gaucher disease recruits Hsp27 to the Hsp90 chaperone complex for proteasomal degradation

Jan 12, 2015 - The Link Between Nutrition, Exercise and Mood

Jan 7, 2015 - Mount Sinai Health System and UC San Diego Partner to Promote Innovation in Emergency Medical Services

Jan 7, 2015 - Rare Diseases and Biomarkers: Challenges and Opportunities

Jan 3, 2015 - 23andMe to offer users' medical data to Pfizer for research

Dec 29, 2014 - Bristol Twp. baby that inspired 'Hannah's Law' passes away

Dec 18, 2014 - The Gift of Nutrition: EPA Helps NC Communities Foster Healthy Food

Dec 17, 2014 - Only 4 in 10 Americans Eat Heart-Healthy Nuts Each Day, CDC Says

Dec 17, 2014 - Year in review: 7 health and nutrition stories of 2014

Dec 17, 2014 - Novel new drugs approved in 2014

Dec 12, 2014 - Other nations also urge govts to create rare disease database

Dec 12, 2014 - Health Ministry working on database for rare diseases

Dec 11, 2014 - Type II NKT-TFH cells against Gaucher lipids regulate B cell immunity and inflammation

Dec 10, 2014 - Quinn on Nutrition: Nourishing gifts for those who need them

Dec 10, 2014 - How many calories do you eat?

Dec 9, 2014 - More menu labeling details emerge

Dec 9, 2014 - A Kid' Nutrition is a Wise Investment

Dec 9, 2014 - Gaucher's Disease Therapeutic Pipeline H2 2014 Review in New Market Research Report

Dec 8, 2014 - A national soda tax is needed to reduce obesity and save lives

Dec 8, 2014 - CLASS Awarded $10,454 from Kansas Health Foundation

Dec 8, 2014 - Each dollar spent on kids' nutrition can yield more than $100 later

Dec 8, 2014 - Health Minute: Better nutrition by age

Dec 8, 2014 - Bigger Regulatory Challenges in Diagnostics Than In Therapeutics Industry, Expert Says

Dec 7, 2014 - Food For Thought... Eat Your Way To Good Health

Dec 7, 2014 - Obesity May Shorten Your Life Expectancy by 8 Years

Dec 7, 2014 - HEALTH AND FITNESS: The truth about holiday weight gain

Dec 7, 2014 - Ohio State signs pact to promote nutrition, physical activity​

Dec 5, 2014 - New Signaling Role for Key Protein May Contribute to Wound Healing, Tumor Growth, Inflammatory Disease

Dec 4, 2014 - €4.5m spent on rare diseases research

Dec 3, 2014 - Genzyme exec: Two big problems facing rare-disease biotechs no one talks about

Dec 1, 2014 - Lysosomal Disease Network November 2014 issue of "Indications"