National Gaucher Foundation - Gaucher Disease
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Gaucher Disease News at a Glance

Jul 18, 2014 - Channel strategy and orphan drugs

Jul 14, 2014 - Drug Firms Make Haste to Elude Tax

Jul 11, 2014 - 21st Century Cures: Incorporating the Patient Perspective U.S. House of Representative Energy and Commerce Committee Subcommittee on Health

Jul 10, 2014 - Tufts study: Orphan drug approvals up, but high costs pose challenges

Jul 2, 2014 - Gaucher drug becomes first to get OU kosher label. Not that the Pfizer medication actually needed kosher certification

Jul 1, 2014 - Gaucher's Disease Pipeline Highlights - 2014 Update

Jun 30, 2014 - Fate Therapeutics Submits IND Application for the Clinical Development of PROHEMA(R) in Inherited Metabolic Disorders

Jun 30, 2014 - Modeling changes in biomarkers in Gaucher disease patients receiving ERT

Jun 27, 2014 - Protalix Announces New Data on ELELYSO(TM) (taliglucerase alfa) Presented at the European Working Group on Gaucher Disease 2014 11th Meeting

Jun 25, 2014 - Genzyme offers inside look at Massachusetts plant under consent decree

Jun 25, 2014 - Villar wants sin taxes to fund rare disease management

Jun 25, 2014 - Class action says Gaucher Disease drug contaminated with virus, caused cancer

Jun 19, 2014 - Illinois newborns to be tested for severe combined immunodeficiency

Jun 19, 2014 - Protalix Enrolls First Gaucher Patient in Phase 2 Trial

Jun 18, 2014 - HHS will enforce disputed rule limiting orphan exclusion from 340B drug discounts

Jun 18, 2014 - Protalix BioTherapeutics Initiates Phase II Study With PRX-112, an Orally-Administered Enzyme Replacement Therapy for the Treatment of Gaucher Disease

Jun 17, 2014 - Patient Claims Genzyme Swapped Good Medicine For Bad

Jun 16, 2014 - Emma Rooney who has Gaucher will begin running a 100km run Friday, June 20 at 11 pm. She is running for fellow Gaucher patients, so give her your support

Jun 13, 2014 - HHS vows to fight for 'orphan drug' rule

Jun 11, 2014 - Gaucher Disease Points Way to Possible New Treatment for Parkinson’s

Jun 10, 2014 - Why Big Pharma Needs Blockbusters

Jun 9, 2014 - Gaucher Disease Carriers Have Higher Parkinson’s Risk

Jun 6, 2014 - The World Market for Orphan Drugs - Markets for Oncology, Hematology, Neurology, Endocrine, Metabolic and Other Drugs

Jun 3, 2014 - FDA Approves SYNERA® (lidocaine and tetracaine) Topical Patch for Home Use

May 30, 2014 - Protalix Announces ELELYSO(TM) (taliglucerase alfa) Approved in Canada for the Treatment of Gaucher Disease in Both Adult and Pediatric Patients

May 28, 2014 - Gaucher's Disease Type I Global Clinical Trials Review, H1, 2014

May 22, 2014 - Protalix Announces ELELYSO(TM) (taliglucerase alfa) Approved in Australia for the Treatment of Gaucher Disease in Both Adult and Pediatric Patients

May 19, 2014 - Chitotriosidase and Gaucher disease severity and progression

May 15, 2014 - FDA and EMA Join Forces on Treatment of Gaucher Disease in Children

May 15, 2014 - Treatments on the Horizon in Multiple Myeloma

May 15, 2014 - Pfizer Inc. Receives Kosher Certification for Elelyso™ for Injection, for the Treatment of Type 1 Gaucher Disease

May 15, 2014 - EMA, FDA to facilitate clinical investigation of new medicines for Gaucher disease in children

May 12, 2014 - Ex-Genzyme CEO’s new company looks to rare diseases for insight into treating Parkinson’s

May 8, 2014 - Gaucher iPSC-derived macrophages produce elevated levels of inflammatory mediators and serve as a new platform for therapeutic development

May 1, 2014 - Shire announces the 2014 Shire ACES Scholarship Program!